Belated congratulations to the newly minted Dr. Bagnell (@abagnell_sci)! She’s going on to do amazing things as a Medical Affairs Postdoctoral Fellow with Sanofi and we miss her dearly!
For #SMAAwarenessMonth 💜 we want to highlight new research offering hope for treating spinal muscular atrophy before birth.
The @MackenzieTippi lab and @SumnerLab found that intra-amniotic delivery of SMN2 ASOs improved survival and motor function in SMA mouse models, surpassing outcomes of postnatal treatment.
Antisense oligonucleotides injected into amniotic fluid led to healthier motor neurons, improved behavior and survival in mouse models of spinal muscular atrophy. @HopkinsMedicine@UCSFMedicinescim.ag/43kciJ4